The New Hope Research Foundation was established as a non-profit organization in 2006 to support scientific research and clinical studies needed to help those neurologically affected by lysosomal storage diseases.  As the initial area of focus, the foundation is conducting and coordinating gene therapy research intent on finding a cure for the hexosaminidase A enzyme deficiency that causes GM2 gangliosidosis, more commonly called Tay-Sachs Disease. Great strides have been made in the scientific understanding of this disease and related gene therapies, but finding a cure will still require extensive scientific research. The New Hope Research Foundation supports this advanced research and has a mission and charter to translate this knowledge into clinical studies and to make effective therapy available to patients.

This web-site is primarily intended for scientists, physicians conducting research, and others interested in scientific research to find cures for neurological aspects of lysosomal storage diseases.

The site is intended to:

• Provide an overview of lysosomal storage diseases and summarize the major challenges of finding treatments or a cure for the central nervous system (CNS) aspects of these diseases,
  
  
• Provide updates on recent research activities being funded by the foundation, and
  
  
• List critical areas for additional medical and scientific research and request research proposals be submitted for funding consideration.

   

 The foundation welcomes comments and recommendations; please do not hesitate to contact us.